Clinical application of base editing for treating -thalassaemia

shared a link

2026-04-08 15:16:17 - Translate -

WWW.NATURE.COM

Nature, Published online: 08 April 2026; doi:10.1038/s41586-026-10342-9A clinical phase1 trial of a single infusion of CS-101, CD34+ cells modified using a transformer base editor to reactivate fetal haemoglobin production, led to early and enduring transfusion independence in patients with -thalassaemia.

0 Comments 0 Shares 2 Views 0 Reviews